The Gene Therapy stream focuses on the critical challenges facing the analysis, characterization, quality control and manufacture of gene therapies for clinical and commercial supply, viral and non-viral-based. Split across two back-to-back tracks, Gene Therapy CMC and Analytics, and Gene Therapy Manufacturing, topics include product and process characterization, CMC, upstream development, molecular biology, potency assays, comparability, emerging analytical technologies, impurities, quality control, comparability, process development, purification, formulation, scale-up and commercial manufacturing. 

Conferences Include:

KEYNOTE PRESENTATIONS

Commercializing Gene Therapies: Balancing Innovation with Patient Access
PANEL MODERATOR:
Susan D'Costa, PhD, CTO, Genezen

Comparability Studies Following Process Change
Scott A. Jeffers, PhD, CTO, Gensight Biologics